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Compound Detail

CHEMBL4594329

CIPAGLUCOSIDASE ALFA
💊 Approved Drug
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💊 Approved Drug
No structure available
ChEMBL ↗

Basic Information

ChEMBL ID CHEMBL4594329
Name CIPAGLUCOSIDASE ALFA
Phase Approved
Structure Type SEQ
Therapeutic ✓ Yes

Known Names

AT GAA ATB-200 ATB200 Cipaglucosidase alfa Cipaglucosidase alfa-atga Pombiliti
0
Targets
0
Activities
0
Assay Types
0
PK Parameters
0
Publications
6
Known Names
3
Indications
1
Mechanisms

Drug Information

Molecule Type Enzyme
First Approval 2023
Availability Prescription
Chirality Single Enantiomer

Routes of Administration

Parenteral

Flags

Black Box Warning
USAN Stem -ase
USAN Year 2019

Mechanism of Action

Mechanism Action Type Target Direct Efficacy
Glycogen hydrolytic enzyme HYDROLYTIC ENZYME Glycogen ✓ ✓

Indications

Glycogen Storage Disease Type II Glycogen Storage Disease Type II Glycogen Storage Disease

ATC Classification

A16AB23
cipaglucosidase alfa
Level 1: ALIMENTARY TRACT AND METABOLISM
Level 2: OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS

Drug Warnings

Black Box Warning
dermatological toxicity
Country: United States
Black Box Warning
respiratory toxicity
Country: United States
Black Box Warning
neurotoxicity
Country: United States

Data from ChEMBL 36 via Core Engine