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Compound Detail

CHEMBL4594335

EPLONTERSEN SODIUM
💊 Approved Drug
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💊 Approved Drug
No structure available

Basic Information

ChEMBL ID CHEMBL4594335
Name EPLONTERSEN SODIUM
Phase Approved
Structure Type SEQ
Therapeutic ✓ Yes

Known Names

AKCEA-TTR-LRX SODIUM Eplontersen sodium ION-682884 ICOSASODIUM SALT ION-682884 SODIUM IONIS-TTR-LRX SODIUM ISIS-682884 Wainua Wainua (autoinjector)
0
Targets
0
Activities
0
Assay Types
0
PK Parameters
0
Publications
8
Known Names
3
Indications
1
Mechanisms

Drug Information

Molecule Type Oligonucleotide
First Approval 2023
Availability Prescription
Chirality Single Enantiomer

Routes of Administration

Parenteral
USAN Stem -rsen

Mechanism of Action

Mechanism Action Type Target Direct Efficacy
Transthyretin mRNA antisense inhibitor ANTISENSE INHIBITOR Transthyretin mRNA

Indications

Amyloid Neuropathies, Familial Polyneuropathies Amyloidosis

Data from ChEMBL 36 via Core Engine