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Assay Detail

CHEMBL5037009

Review assay metadata, readout intent, target linkage, and publication context from the same page.

Binding
Potentiation of CFTR F508del mutant (unknown origin) expressed in CHO cells assessed as chloride transport by measuring membrane potential incubated for 5 to 30 mins in presence of forskolin by Quattro assay
33
Total Activities
30
Compounds Tested
1
Activity Types
0
Assay Parameters

Assay Information

Assay Type Binding
Organism Homo sapiens
Cell Type CHO
Confidence 9 — Direct single protein target
Curated By Autocuration

Target

Cystic fibrosis transmembrane conductance regulator (CHEMBL4051)
Type SINGLE PROTEIN
Organism Homo sapiens

Publication

Discovery of Icenticaftor (QBW251), a Cystic Fibrosis Transmembrane Conductance Regulator Potentiator with Clinical Efficacy in Cystic Fibrosis and Chronic Obstructive Pulmonary Disease.
Grand DL, Gosling M, Baettig U, Bahra P, Bala K, Brocklehurst C, Budd E, Butler R, Cheung AK, Choudhury H, Collingwood SP, Cox B, Danahay H, Edwards L, Everatt B, Glaenzel U, Glotin AL, Groot-Kormelink P, Hall E, Hatto J, Howsham C, Hughes G, King A, Koehler J, Kulkarni S, Lightfoot M, Nicholls I, Page C, Pergl-Wilson G, Popa MO, Robinson R, Rowlands D, Sharp T, Spendiff M, Stanley E, Steward O, Taylor RJ, Tranter P, Wagner T, Watson H, Williams G, Wright P, Young A, Sandham DA.
J Med Chem (2021) 64 : 7241 -7260
PubMed 34028270 · DOI

Activity Statistics

Type Count Avg pChEMBL Best pChEMBL
EC50 33 6.74 8.10

Compounds Tested

Compound Name Phase Activities Best pChEMBL
CHEMBL5076312 2 8.10
CHEMBL5088607 1 8.05
CHEMBL5087757 1 8.05
CHEMBL5075860 1 8.00
CHEMBL5075769 1 7.82
CHEMBL5084140 1 7.82
CHEMBL5082569 2 7.70
CHEMBL5081202 1 7.64
CHEMBL5088068 1 7.52
CHEMBL5093146 1 7.40
CHEMBL4650318 ICENTICAFTOR 2.0 1 7.33
CHEMBL5082261 1 7.16
CHEMBL5080252 1 7.11
CHEMBL5071764 1 7.11
CHEMBL5075105 2 6.96
CHEMBL5079547 1 6.64
CHEMBL5083308 1 6.62
CHEMBL5085939 1 6.62
CHEMBL5086285 1 6.60
CHEMBL5076850 1 6.48
CHEMBL5083598 1 6.44
CHEMBL5091133 1 6.33
CHEMBL1949980 1 5.90
CHEMBL5085049 1 5.73
CHEMBL5085731 1 5.42
CHEMBL5085858 1 5.28
CHEMBL5077730 1 5.23
CHEMBL44 GENISTEIN 2.0 1 5.07
CHEMBL1493986 METHYL ANTHRANILATE 1 4.52
CHEMBL5077005 1 4.52

Activity Data

Compound Name Type Rel. Value Units pChEMBL
CHEMBL5076312 EC50 = 8.0 nM 8.10
CHEMBL5088607 EC50 = 9.0 nM 8.05
CHEMBL5087757 EC50 = 9.0 nM 8.05
CHEMBL5075860 EC50 = 10.0 nM 8.00
CHEMBL5075769 EC50 = 15.0 nM 7.82
CHEMBL5084140 EC50 = 15.0 nM 7.82
CHEMBL5082569 EC50 = 20.0 nM 7.70
CHEMBL5081202 EC50 = 23.0 nM 7.64
CHEMBL5088068 EC50 = 30.0 nM 7.52
CHEMBL5093146 EC50 = 40.0 nM 7.40
CHEMBL5076312 EC50 = 43.0 nM 7.37
CHEMBL5082569 EC50 = 46.0 nM 7.34
CHEMBL4650318 ICENTICAFTOR EC50 = 47.0 nM 7.33
CHEMBL5082261 EC50 = 70.0 nM 7.16
CHEMBL5080252 EC50 = 78.0 nM 7.11
CHEMBL5071764 EC50 = 77.0 nM 7.11
CHEMBL5075105 EC50 = 111.0 nM 6.96
CHEMBL5079547 EC50 = 229.0 nM 6.64
CHEMBL5083308 EC50 = 240.0 nM 6.62
CHEMBL5085939 EC50 = 240.0 nM 6.62
CHEMBL5086285 EC50 = 250.0 nM 6.60
CHEMBL5075105 EC50 = 276.0 nM 6.56
CHEMBL5076850 EC50 = 329.0 nM 6.48
CHEMBL5083598 EC50 = 362.0 nM 6.44
CHEMBL5091133 EC50 = 462.0 nM 6.33
CHEMBL1949980 EC50 = 1250.0 nM 5.90
CHEMBL5085049 EC50 = 1860.0 nM 5.73
CHEMBL5085731 EC50 = 3780.0 nM 5.42
CHEMBL5085858 EC50 = 5310.0 nM 5.28
CHEMBL5077730 EC50 = 5830.0 nM 5.23
CHEMBL44 GENISTEIN EC50 = 8480.0 nM 5.07
CHEMBL1493986 METHYL ANTHRANILATE EC50 = 30000.0 nM 4.52
CHEMBL5077005 EC50 = 30000.0 nM 4.52