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Compound Detail

CHEMBL354077

AMIFAMPRIDINE
💊 Approved Drug
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💊 Approved Drug

Basic Information

ChEMBL ID CHEMBL354077
Name AMIFAMPRIDINE
Phase Approved
Structure Type MOL
InChI Key OYTKINVCDFNREN-UHFFFAOYSA-N
Therapeutic ✓ Yes

Known Names

3,4-DAP 3,4-diammoniopyridinium 4-DAP Amifampridina Amifampridine DAP Dynamine NSC-521760 Pyridine-3,4-diamine Ruzurgi
0
Targets
1
Activities
1
Assay Types
1
PK Parameters
20
Publications
10
Known Names
5
Indications
1
Mechanisms

Molecular Properties

109.1
MW (Da)
0.25
ALogP
3
HBA
2
HBD
64.9
PSA (Ų)
0.50
QED
0
Ro5 Violations
0
Rot. Bonds

Drug Information

Molecule Type Small molecule
First Approval 2009
Availability Prescription
Chirality Achiral

Routes of Administration

Oral

Flags

Natural Product
USAN Year 2014

Extended Properties

Molecular Formula C5H7N3
MW 109.13
Aromatic Rings 1
Heavy Atoms 8
NP-Likeness -0.66

Mechanism of Action

Mechanism Action Type Target Direct Efficacy
Voltage-gated potassium channel blocker BLOCKER Voltage-gated potassium channel

Indications

Lambert-Eaton Myasthenic Syndrome Lambert-Eaton Myasthenic Syndrome Multiple Sclerosis Myasthenia Gravis Botulism

ATC Classification

N07XX05
amifampridine
Level 1: NERVOUS SYSTEM
Level 2: OTHER NERVOUS SYSTEM DRUGS

Activity Summary

Ki 1 meas.

Pharmacokinetic Data

Parameter Value Units Species
CL 18.8 mL.min-1.g-1 Homo sapiens

Literature References

PubMed DOI Target Context # Activities
- 10.1016/S0960-894X(00)80544-2 Rattus norvegicus 24
- 10.6019/CHEMBL4495565 SARS-CoV-2 4
37468498 10.1038/s41467-023-40064-9 Muscarinic acetylcholine receptor M1 3
37468498 10.1038/s41467-023-40064-9 Alpha-1A adrenergic receptor 3
33606526 10.1021/acs.jmedchem.0c02047 POU domain, class 2, transcription factor 1 3
37468498 10.1038/s41467-023-40064-9 D(1A) dopamine receptor 2
37468498 10.1038/s41467-023-40064-9 Thromboxane A2 receptor 2
37468498 10.1038/s41467-023-40064-9 Prostaglandin G/H synthase 1 2
- 10.6019/CHEMBL4808148 Histone deacetylase 6 2
- 10.6019/CHEMBL4651402 SARS-CoV-2 2
- 10.6019/CHEMBL4495564 Replicase polyprotein 1ab 2
33606526 10.1021/acs.jmedchem.0c02047 Unchecked 1
37468498 10.1038/s41467-023-40064-9 Voltage-gated inwardly rectifying potassium channel KCNH2 1
37468498 10.1038/s41467-023-40064-9 Sodium-dependent dopamine transporter 1
37468498 10.1038/s41467-023-40064-9 Estrogen receptor 1
37468498 10.1038/s41467-023-40064-9 Acetylcholinesterase 1
37468498 10.1038/s41467-023-40064-9 Sodium-dependent noradrenaline transporter 1
37468498 10.1038/s41467-023-40064-9 Alpha-2A adrenergic receptor 1
37468498 10.1038/s41467-023-40064-9 Mu-type opioid receptor 1
- 10.21203/rs.3.rs-23951/v1 SARS-CoV-2 1

Data from ChEMBL 36 via Core Engine