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Compound Detail

CHEMBL363392

MARALIXIBAT
💊 Approved Drug
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💊 Approved Drug
CCCCC1(CCCC)CS(=O)(=O)c2ccc(N(C)C)cc2[C@@H](c2ccc(OCc3ccc(C[N+]45CCN(CC4)CC5)cc3)cc2)[C@H]1O

Basic Information

ChEMBL ID CHEMBL363392
Name MARALIXIBAT
Phase Approved
Structure Type MOL
InChI Key STPKWKPURVSAJF-LJEWAXOPSA-N
Therapeutic ✓ Yes

Known Names

Lopixibat LUM-001 CATION LUM001 CATION Maralixibat Maralixibat cation TAK-625
1
Targets
2
Activities
1
Assay Types
2
PK Parameters
4
Publications
6
Known Names
3
Indications
1
Mechanisms

Molecular Properties

675.0
MW (Da)
6.62
ALogP
6
HBA
1
HBD
70.1
PSA (Ų)
0.21
QED
2
Ro5 Violations
13
Rot. Bonds

Drug Information

Molecule Type Small molecule
First Approval 2021
Availability Prescription
Chirality Single Enantiomer

Routes of Administration

Oral
USAN Stem -ixibat
USAN Year 2016

Extended Properties

Molecular Formula C40H56N3O4S+
MW 674.97
Aromatic Rings 3
Heavy Atoms 48
NP-Likeness -0.25

Mechanism of Action

Mechanism Action Type Target Direct Efficacy
Ileal bile acid transporter inhibitor INHIBITOR Ileal sodium/bile acid cotransporter

Indications

Alagille Syndrome Biliary Atresia Liver Diseases

Activity Summary

IC50 2 meas. best 9.55

Target Activity Profile

Target Type Best pChEMBL Mean pChEMBL Best (nM) # Data
Ileal sodium/bile acid cotransporter
CHEMBL2778
IC50 9.55 9.55 0.3 2

Pharmacokinetic Data

Parameter Value Units Species
Cmax - nM Rattus norvegicus
Cmax - nM Rattus norvegicus

Activity Data Samples

Top measurements by pChEMBL value

Literature References

PubMed DOI Target Context # Activities
16134951 10.1021/jm0402162 ADMET 4
16134951 10.1021/jm0402162 Ileal sodium/bile acid cotransporter 1
36923921 10.1021/acsmedchemlett.3c00001 ADMET 1
36923921 10.1021/acsmedchemlett.3c00001 Ileal sodium/bile acid cotransporter 1

Data from ChEMBL 36 via Core Engine