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Compound Detail

CHEMBL5314934

VANZACAFTOR
💊 Approved Drug
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💊 Approved Drug
CC1(C)C[C@@H]2CCCNc3cccc(n3)S(=O)(=O)NC(=O)c3ccc(-n4ccc(OCCC5C6(CC6)C56CC6)n4)nc3N1C2

Basic Information

ChEMBL ID CHEMBL5314934
Name VANZACAFTOR
Phase Approved
Structure Type MOL
InChI Key VCSUIBJKYCVWNF-NRFANRHFSA-N
Therapeutic ✓ Yes

Known Names

Vanzacaftor Vanzacaftor component of alyftrek Vx-121
0
Targets
0
Activities
0
Assay Types
0
PK Parameters
0
Publications
3
Known Names
1
Indications
1
Mechanisms

Molecular Properties

617.8
MW (Da)
4.55
ALogP
10
HBA
2
HBD
131.3
PSA (Ų)
0.42
QED
1
Ro5 Violations
5
Rot. Bonds

Drug Information

Molecule Type Small molecule
First Approval 2024
Availability Prescription
Chirality Single Enantiomer

Routes of Administration

Oral
USAN Stem -caftor
USAN Year 2023

Extended Properties

Molecular Formula C32H39N7O4S
MW 617.78
Aromatic Rings 3
Heavy Atoms 44
NP-Likeness -0.21

Mechanism of Action

Mechanism Action Type Target Direct Efficacy
Cystic fibrosis transmembrane conductance regulator positive modulator POSITIVE MODULATOR Cystic fibrosis transmembrane conductance regulator

Indications

Cystic Fibrosis

Data from ChEMBL 36 via Core Engine